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doi:10.1016/j.omtn.2017.02.004
Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System
Annalisa Lattanzi
Stephanie Duguez
Arianna Moiani
Araksya Izmiryan
Elena Barbon
Samia Martin
Kamel Mamchaoui
Vincent Mouly
Francesco Bernardi
Fulvio Mavilio
Matteo Bovolenta
dystrophin
CRISPR/Cas9
duplication
lentivirus
gene editing
Molecular Therapy: Nucleic Acid, 7 (2017) 11-19. doi:10.1016/j.omtn.2017.02.004
Elsevier Ltd.
journal
Molecular Therapy: Nucleic Acid
© 2017 The Author(s).
2162-2531
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2017-06-16
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