Quantitative antisense screening and optimization for exon 51 skipping in Duchenne muscular dystrophy

Yusuke Echigoya, Kenji Rowel Q. Lim, Nhu Trieu, Bo Bao, Bailey Miskew, Maria Candida Vila, James S. Novak, Yuko Hara, Joshua Lee, Aleksander Touznik, Kamel Mamchaoui, Yoshitsugu Aoki, Shin'ichi Takeda, Kanneboyina Nagaraju, Vincent Mouly, Rika Maruyama, William Duddy, Toshifumi Yokota

Research output: Contribution to journalArticle

22 Citations (Scopus)
LanguageEnglish
Pages2561-2572
Number of pages11
JournalMolecular Therapy
Volume25
Issue number11
DOIs
Publication statusPublished - 28 Jul 2017

Keywords

  • exon skipping
  • duchenne
  • muscular dystrophy
  • computational biology

Cite this

Echigoya, Y., Lim, K. R. Q., Trieu, N., Bao, B., Miskew, B., Vila, M. C., ... Yokota, T. (2017). Quantitative antisense screening and optimization for exon 51 skipping in Duchenne muscular dystrophy. Molecular Therapy, 25(11), 2561-2572. https://doi.org/10.1016/j.ymthe.2017.07.014
Echigoya, Yusuke ; Lim, Kenji Rowel Q. ; Trieu, Nhu ; Bao, Bo ; Miskew, Bailey ; Vila, Maria Candida ; Novak, James S. ; Hara, Yuko ; Lee, Joshua ; Touznik, Aleksander ; Mamchaoui, Kamel ; Aoki, Yoshitsugu ; Takeda, Shin'ichi ; Nagaraju, Kanneboyina ; Mouly, Vincent ; Maruyama, Rika ; Duddy, William ; Yokota, Toshifumi. / Quantitative antisense screening and optimization for exon 51 skipping in Duchenne muscular dystrophy. In: Molecular Therapy. 2017 ; Vol. 25, No. 11. pp. 2561-2572.
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title = "Quantitative antisense screening and optimization for exon 51 skipping in Duchenne muscular dystrophy",
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author = "Yusuke Echigoya and Lim, {Kenji Rowel Q.} and Nhu Trieu and Bo Bao and Bailey Miskew and Vila, {Maria Candida} and Novak, {James S.} and Yuko Hara and Joshua Lee and Aleksander Touznik and Kamel Mamchaoui and Yoshitsugu Aoki and Shin'ichi Takeda and Kanneboyina Nagaraju and Vincent Mouly and Rika Maruyama and William Duddy and Toshifumi Yokota",
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Echigoya, Y, Lim, KRQ, Trieu, N, Bao, B, Miskew, B, Vila, MC, Novak, JS, Hara, Y, Lee, J, Touznik, A, Mamchaoui, K, Aoki, Y, Takeda, S, Nagaraju, K, Mouly, V, Maruyama, R, Duddy, W & Yokota, T 2017, 'Quantitative antisense screening and optimization for exon 51 skipping in Duchenne muscular dystrophy', Molecular Therapy, vol. 25, no. 11, pp. 2561-2572. https://doi.org/10.1016/j.ymthe.2017.07.014

Quantitative antisense screening and optimization for exon 51 skipping in Duchenne muscular dystrophy. / Echigoya, Yusuke; Lim, Kenji Rowel Q.; Trieu, Nhu; Bao, Bo; Miskew, Bailey; Vila, Maria Candida; Novak, James S.; Hara, Yuko; Lee, Joshua; Touznik, Aleksander; Mamchaoui, Kamel; Aoki, Yoshitsugu; Takeda, Shin'ichi; Nagaraju, Kanneboyina; Mouly, Vincent; Maruyama, Rika; Duddy, William; Yokota, Toshifumi.

In: Molecular Therapy, Vol. 25, No. 11, 28.07.2017, p. 2561-2572.

Research output: Contribution to journalArticle

TY - JOUR

T1 - Quantitative antisense screening and optimization for exon 51 skipping in Duchenne muscular dystrophy

AU - Echigoya, Yusuke

AU - Lim, Kenji Rowel Q.

AU - Trieu, Nhu

AU - Bao, Bo

AU - Miskew, Bailey

AU - Vila, Maria Candida

AU - Novak, James S.

AU - Hara, Yuko

AU - Lee, Joshua

AU - Touznik, Aleksander

AU - Mamchaoui, Kamel

AU - Aoki, Yoshitsugu

AU - Takeda, Shin'ichi

AU - Nagaraju, Kanneboyina

AU - Mouly, Vincent

AU - Maruyama, Rika

AU - Duddy, William

AU - Yokota, Toshifumi

PY - 2017/7/28

Y1 - 2017/7/28

KW - exon skipping

KW - duchenne

KW - muscular dystrophy

KW - computational biology

U2 - 10.1016/j.ymthe.2017.07.014

DO - 10.1016/j.ymthe.2017.07.014

M3 - Article

VL - 25

SP - 2561

EP - 2572

JO - Molecular Therapy

T2 - Molecular Therapy

JF - Molecular Therapy

SN - 1525-0024

SN - 1525-0016

IS - 11

ER -