Skip to main navigation Skip to search Skip to main content

Potential of oligonucleotide-mediated exon-skipping therapy for Duchenne muscular dystrophy

  • Toshifumi Yokota
  • , Emidio Pistilli
  • , William Duddy
  • , Kanneboyina Nagaraju

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)831-842
JournalExpert Opinion on Biological Therapy
Volume7
Issue number6
Publication statusPublished (in print/issue) - 2007

Keywords

  • Duchenne muscular dystrophy
  • antisense oligonucleotides
  • morpholinos
  • exon skipping

Cite this