Potential of oligonucleotide-mediated exon-skipping therapy for Duchenne muscular dystrophy

Toshifumi Yokota, Emidio Pistilli, William Duddy, Kanneboyina Nagaraju

Research output: Contribution to journalArticlepeer-review

51 Citations (Scopus)
Original languageEnglish
Pages (from-to)831-842
JournalExpert Opinion on Biological Therapy
Issue number6
Publication statusPublished (in print/issue) - 2007


  • Duchenne muscular dystrophy
  • antisense oligonucleotides
  • morpholinos
  • exon skipping

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