Optimizing exon skipping therapies for DMD

T Yokota, William Duddy, T Partridge

Research output: Contribution to journalArticlepeer-review

70 Citations (Scopus)
Original languageEnglish
Pages (from-to)179
JournalActa Myologica
Volume26
Issue number3
Publication statusPublished (in print/issue) - 2007

Keywords

  • Duchenne/Becker muscular dystrophy
  • dystrophin
  • revertant fibers
  • morpholinos

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