Gene therapy with AR isoform 2 rescues spinal and bulbar muscular atrophy phenotype 2 by modulating AR transcriptional activity: AR isoform 2 counteracts polyglutamine AR toxicity

Wooi F. Lim, Mitra Forouhan, Thomas C Roberts, Jesse Dabney, Ruth Ellerington, Alfina A Speciale, Raquel Manzano, Maria Lieto, Gavinda Sangha, Subhashis Banerjee, Mariana Conceicao, Lara Cravo, Anabelle Biscans, Loic Roux, Naemeh Pourshafle, Christopher Grunseich, Stephanie Duguez, Anastasia Khvorova, Maria Pennuto, Constanza J CortesAlbert R La Spada, Kenneth H Fischbeck, Matthew JA Wood, Carlo RinaldiShow 4 moreShow less