Exon skipping for nonsense mutations in Duchenne muscular dystrophy: too many mutations, too few patients?

Toshifumi Yokota, William Duddy, Yusuke Echigoya, Hanna Kolski

Research output: Contribution to journalArticlepeer-review

30 Citations (Scopus)
23 Downloads (Pure)
Original languageEnglish
Pages (from-to)1141-1152
JournalExpert Opinion on Biological Therapy
Volume12
Issue number9
Publication statusPublished - 2012

Keywords

  • Exon skipping
  • muscular dystrophy
  • duchenne
  • nonsense mutations

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