Development of Allele-Specific Therapeutic siRNA for Keratin 5 Mutations in Epidermolysis Bullosa Simplex.

Sarah Atkinson, Victoria McGilligan, H Liao, I Szeverenyi, FJ Smith, Tara Moore, WH McLean

Research output: Contribution to journalArticlepeer-review

67 Citations (Scopus)

Fingerprint

Dive into the research topics of 'Development of Allele-Specific Therapeutic siRNA for Keratin 5 Mutations in Epidermolysis Bullosa Simplex.'. Together they form a unique fingerprint.

Biochemistry, Genetics and Molecular Biology

Pharmacology, Toxicology and Pharmaceutical Science

Immunology and Microbiology